RG7800

small molecule SMN2 splicing modifier

Also Known As:

2-(4-ethyl-6-methylpyrazolo(1,5-a)pyrazin-2-yl)-9-methyl-7-(1-methylpiperidin-4-yl)pyrido(1,2-a)pyrimidin-4-one; RO6885247

Networked: 1 relevant articles (0 outcomes, 1 trials/studies)

1.	Birkhoff, Willem: 1 article (01/2019)
2.	Bugawan, Teodorica: 1 article (01/2019)
3.	Czech, Christian: 1 article (01/2019)
4.	Dziadek, Sebastian: 1 article (01/2019)
5.	Fischer, Dirk: 1 article (01/2019)
6.	Gerlach, Irene: 1 article (01/2019)
7.	Groeneveld, Geert Jan: 1 article (01/2019)
8.	Günther, Andreas: 1 article (01/2019)
9.	Heinig, Katja: 1 article (01/2019)
10.	Heuberger, Jules: 1 article (01/2019)

1.	Spinal Muscular Atrophy (Progressive Muscular Atrophy) 01/01/2019 - "The oral splicing modifier RG7800 increases full length survival of motor neuron 2 mRNA and survival of motor neuron protein: Results from trials in healthy adults and patients with spinal muscular atrophy."