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Enzyme Replacement Therapy

Therapeutic replacement or supplementation of defective or missing enzymes to alleviate the effects of enzyme deficiency (e.g., GLUCOSYLCERAMIDASE replacement for GAUCHER DISEASE).
Also Known As:
Enzyme Replacement Therapies; Replacement Therapies, Enzyme; Replacement Therapy, Enzyme; Therapies, Enzyme Replacement; Therapy, Enzyme Replacement
Networked: 2992 relevant articles (373 outcomes, 338 trials/studies)

Relationship Network

Therapy Context: Research Results

Experts

1. Kishnani, Priya S: 86 articles (09/2022 - 08/2005)
2. Zimran, Ari: 61 articles (01/2022 - 01/2002)
3. Giugliani, Roberto: 59 articles (01/2022 - 06/2005)
4. Elstein, Deborah: 45 articles (01/2018 - 01/2002)
5. van der Ploeg, Ans T: 43 articles (12/2022 - 06/2003)
6. Beck, Michael: 42 articles (01/2022 - 06/2002)
7. Schiffmann, Raphael: 38 articles (09/2021 - 03/2002)
8. Wanner, Christoph: 35 articles (06/2022 - 01/2003)
9. Hollak, Carla E M: 31 articles (01/2020 - 04/2006)
10. Harmatz, Paul: 30 articles (01/2021 - 05/2004)

Related Diseases

1. Glycogen Storage Disease Type II (Pompe's Disease)
2. Gaucher Disease (Gaucher's Disease)
3. Fabry Disease (Fabry's Disease)
4. Mucopolysaccharidosis I (Hurler Syndrome)
5. Mucopolysaccharidoses

Related Drugs and Biologics

1. human GAA protein (Myozyme)
2. Enzymes
3. idursulfase
4. Glucosylceramidase (Glucocerebrosidase)
5. Acids
6. imiglucerase
7. Biomarkers (Surrogate Marker)
8. alglucerase
9. Mannose (D-Mannose)
10. agalsidase alfa

Related Therapies and Procedures

1. Therapeutics
2. Bone Marrow Transplantation (Transplantation, Bone Marrow)
3. Intravenous Infusions
4. Mechanical Ventilators (Ventilator)
5. Hematopoietic Stem Cell Transplantation