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Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker)

An X-linked recessive muscle disease caused by an inability to synthesize DYSTROPHIN, which is involved with maintaining the integrity of the sarcolemma. Muscle fibers undergo a process that features degeneration and regeneration. Clinical manifestations include proximal weakness in the first few years of life, pseudohypertrophy, cardiomyopathy (see MYOCARDIAL DISEASES), and an increased incidence of impaired mentation. Becker muscular dystrophy is a closely related condition featuring a later onset of disease (usually adolescence) and a slowly progressive course. (Adams et al., Principles of Neurology, 6th ed, p1415)
Also Known As:
Muscular Dystrophy, Becker; Becker Muscular Dystrophy; Muscular Dystrophy, Duchenne; Becker's Muscular Dystrophy; Cardiomyopathy, Dilated, 3B; Cardiomyopathy, Dilated, X-Linked; Childhood Muscular Dystrophy, Pseudohypertrophic; Childhood Pseudohypertrophic Muscular Dystrophy; Duchenne and Becker Muscular Dystrophy; Duchenne-Becker Muscular Dystrophy; Duchenne-Type Progressive Muscular Dystrophy; Muscular Dystrophy Pseudohypertrophic Progressive, Becker Type; Muscular Dystrophy, Becker Type; Muscular Dystrophy, Childhood, Pseudohypertrophic; Muscular Dystrophy, Duchenne Type; Muscular Dystrophy, Duchenne and Becker Types; Muscular Dystrophy, Pseudohypertrophic Progressive, Becker Type; Muscular Dystrophy, Pseudohypertrophic Progressive, Duchenne Type; Muscular Dystrophy, Pseudohypertrophic, Childhood; Progressive Muscular Dystrophy, Duchenne Type; Pseudohypertrophic Childhood Muscular Dystrophy; Pseudohypertrophic Muscular Dystrophy, Childhood; Duchenne Becker Muscular Dystrophy; Duchenne Type Progressive Muscular Dystrophy; Muscular Dystrophy, Becker's; Muscular Dystrophy, Duchenne-Becker; Pseudohypertrophic Muscular Dystrophy; Muscular Dystrophy, Pseudohypertrophic
Networked: 6464 relevant articles (250 outcomes, 651 trials/studies)

Relationship Network

Disease Context: Research Results

Related Diseases

1. Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker)
2. Cardiomyopathies (Cardiomyopathy)
3. Muscular Dystrophies (Muscular Dystrophy)
4. Disease Progression
5. Fibrosis (Cirrhosis)

Experts

1. Muntoni, Francesco: 94 articles (08/2022 - 07/2002)
2. Takeda, Shin'ichi: 84 articles (01/2022 - 03/2002)
3. Aartsma-Rus, Annemieke: 73 articles (01/2022 - 10/2002)
4. Hoffman, Eric P: 70 articles (01/2022 - 04/2002)
5. Yokota, Toshifumi: 68 articles (02/2022 - 05/2002)
6. Matsuo, Masafumi: 67 articles (01/2022 - 01/2002)
7. Duan, Dongsheng: 62 articles (01/2022 - 03/2002)
8. McDonald, Craig M: 57 articles (12/2022 - 09/2010)
9. Davies, Kay E: 54 articles (10/2022 - 04/2002)
10. Chamberlain, Jeffrey S: 53 articles (01/2022 - 03/2002)

Drugs and Biologics

Drugs and Important Biological Agents (IBA) related to Duchenne Muscular Dystrophy:
1. DystrophinIBA
2. Adrenal Cortex Hormones (Corticosteroids)IBA
3. Antisense OligonucleotidesIBA
4. GlucocorticoidsIBA
5. SteroidsIBA
6. Proteins (Proteins, Gene)FDA Link
7. MorpholinosIBA
8. Creatine Kinase (Creatine Phosphokinase)IBA
9. Prednisolone (Predate)FDA LinkGeneric
10. Prednisone (Sone)FDA LinkGeneric

Therapies and Procedures

1. Therapeutics
2. Artificial Respiration (Mechanical Ventilation)
3. Transplantation
4. Cell- and Tissue-Based Therapy (Cell Therapy)
5. Ligation