| Abstract | OBJECTIVE: To evaluate the effectiveness of low oral doses of methotrexate as a steroid-sparing agent in children with sarcoidosis. STUDY DESIGN: An open-label, noncontrolled trial. Methotrexate was administered orally at a single weekly dose of 10 to 15 mg/m2. Duration of therapy was open ended, but patients received treatment for a minimum of 6 months to be considered as having completed the study. RESULTS: Seven children with biopsy-proven sarcoidosis completed the study. The mean dose of prednisone was successfully tapered from 49 mg/day (1.3 mg/kg) to 18 mg/day (0.5 mg/kg) after 3 months of methotrexate therapy and to 9.9 (0.2 mg/kg) and 7.3 mg/day (0.1 mg/kg) after 6 months and at the end of the follow-up period, respectively. Other clinical and laboratory parameters improved significantly after methotrexate therapy was started. There was significant clinical improvement, as confirmed by the reduction of the clinical severity score from 8 +/- 1.1 to 0.8 +/- 0.5 point after 3 months of methotrexate therapy, and to 0.7 and 0.5 +/- 0.3 point after 6 months and at the end of the follow-up, respectively. Laboratory measurements revealed marked improvement, as reflected by a significant reduction in the erythrocyte sedimentation rate and an increase of hemoglobin values. The mean serum angiotensin-converting enzyme activity dropped significantly. No adverse side effects were noted with methotrexate therapy.CONCLUSION: Our study demonstrated that low-dose oral methotrexate therapy was effective and safe and had steroid-sparing properties in seven children with sarcoidosis. |
| Authors | A Gedalia, J F Molina, G S Ellis Jr, W Galen, C Moore, L R Espinoza
(Affiliation: Division of Pediatric Rheumatology, Children's Hospital, New Orleans, Louisiana State University Medical Center 70112-2822, USA.)
|
| Journal | The Journal of pediatrics
(J Pediatr)
Vol. 130
Issue 1
Pg. 25-9
(Jan 1997)
ISSN: 0022-3476 UNITED STATES |
| PMID | 9003847
(Publication Type: Clinical Trial, Journal Article)
|
| Chemical References |
- Glucocorticoids
- Prednisone
- Methotrexate
|
| Topics |
- Administration, Oral
- Child
- Drug Administration Schedule
- Drug Therapy, Combination
- Female
- Follow-Up Studies
- Glucocorticoids
(therapeutic use)
- Humans
- Male
- Methotrexate
(administration & dosage, therapeutic use)
- Prednisone
(therapeutic use)
- Sarcoidosis
(classification, drug therapy)
- Severity of Illness Index
- Treatment Outcome
|