Abstract | BACKGROUND: CASE PRESENTATION: CONCLUSIONS: We report on two Fabry disease patients who experienced severe adverse events while on approved and/or reduced doses of agalsidase beta. Switching to agalsidase alfa associated with standard care in heart disease led to resolution or improvement in the cardiorespiratory status. And reduction in dose associated with standard care in respiratory disease was useful for decrease in cough and fatigue. Plasma BNP level was useful for monitoring heart failure and the effects of ERT.
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Authors | Kazuya Tsuboi, Hiroshi Yamamoto, Fuji Somura, Hiromi Goto |
Journal | JIMD reports
(JIMD Rep)
Vol. 15
Pg. 105-11
( 2015)
ISSN: 2192-8304 [Print] United States |
PMID | 24718841
(Publication Type: Journal Article)
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