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Multiple Acyl Coenzyme A Dehydrogenase Deficiency
Summary
80
relevant articles (3 outcomes,
4 trials/studies)
found for this Disease
Description:
An autosomal recessive disorder of fatty acid oxidation, and branched chain amino acids (AMINO ACIDS, BRANCHED-CHAIN); LYSINE; and CHOLINE catabolism, that is due to defects in either subunit of ELECTRON TRANSFER FLAVOPROTEIN or its dehydrogenase, electron transfer flavoprotein-ubiquinone oxidoreductase (EC 1.5.5.1).
Also Known As:
ETFA Deficiency; ETFB Deficiency; ETFDH Deficiency; Electron Transfer Flavoprotein Alpha Subunit Deficiency; Electron Transfer Flavoprotein Beta Subunit Deficiency Show All >>
Key Drugs and Agents for Multiple Acyl Coenzyme A Dehydrogenase Deficiency
Efficacy Chart >>
Drugs and Important Biological Agents (IBA) related to treatments:
-
Riboflavin (Vitamin B2)
:
1 outcome in 17 results
:
FDA 8
-
Carnitine (L-Carnitine)
:
1 outcome in 13 results
:
FDA 9
Generic
-
Mitochondrial Proteins (Mitochondrial Protein)
:
1 outcome in 1 result
: IBA
-
Glycine (Aminoacetic Acid)
:
1 outcome in 1 result
:
FDA 30
Generic
-
CAV protocol (CHO)
:
1 outcome in 1 result
:
FDA 1
-
Acyl Coenzyme A (Acyl CoA)
:
1 study in 16 results
: IBA
-
Electron-Transferring Flavoproteins (Electron Transfer Flavoprotein)
:
1 study in 11 results
: IBA
-
electron-transferring-flavoprotein dehydrogenase (ETF dehydrogenase)
:
1 study in 6 results
: IBA
-
Acyl-CoA Dehydrogenases
:
1 study in 4 results
: IBA
-
Sarcosine (Methylglycine)
:
1 study in 3 results
: IBA
Show All >>
Diseases Related to Multiple Acyl Coenzyme A Dehydrogenase Deficiency
-
Muscle Weakness
-
Multiple Acyl Coenzyme A Dehydrogenase Deficiency
-
Muscular Diseases (Myopathy)
-
Multiple Carboxylase Deficiency (Deficiency, Multiple Carboxylase)
-
Polycystic Kidney Diseases (Polycystic Kidney Disease)
Show All >>
Key Therapies for Multiple Acyl Coenzyme A Dehydrogenase Deficiency
Efficacy Chart >>
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